The National Academies of Sciences, Engineering and Medicine
Office of Congressional and government Affairs
At A Glance
 
 
Briefing
: Rare Diseases and Orphan Products: Accelerating Research and Development
Dates:
Thu, Oct 28, 2010   430 Dirksen Senate Office Bldg. – 11:00 a.m.

 

THE NATIONAL ACADEMIES
Institute of Medicine
Board on Health Sciences Policy
Committee on Accelerating Rare Diseases Research and Orphan Product Development

*****

Congressional Briefing

on

Rare Diseases and Orphan Products: Accelerating Research and Development

While the number of people affected by each rare disease is relatively small, the number of these diseases is so large -- an estimated 5,000 to 8,000 conditions -- that a host of challenges complicates the development of safe and effective drugs, biologics, and medical devices to prevent, diagnose, treat, or cure these conditions. This report recommends an integrated national strategy to improve rare disease research and product development.

This briefing was for members of Congress and congressional staff only. The report was publicly released on October 4, 2010 and can be found, in its entirety, on the Web site of the National Academies Press.