Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop (2019)

Chapter: 3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges

Previous Chapter: 2 Exploring the Current Landscape of Central Nervous System Gene-Targeted Therapies
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

There was a problem loading page 23.

Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

There was a problem loading page 24.

Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

There was a problem loading page 25.

Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.

There was a problem loading page 26.

Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 18
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
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Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 20
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 21
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 22
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 23
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 24
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
Page 25
Suggested Citation: "3 Gene-Targeted Therapy Approaches for Central Nervous System Disorders: Opportunities and Challenges." National Academies of Sciences, Engineering, and Medicine. 2019. Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop. Washington, DC: The National Academies Press. doi: 10.17226/25529.
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Next Chapter: 4 Translating Gene-Targeted Therapies from Bench to Bedside
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